Gene Therapy for Cystic Fibrosis What is cystic fibrosis?
Cystic fibrosis (CF) is a rare genetic disorder that affects the lungs, digestive system, and other organs. It is caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene, which encodes a protein that regulates chloride ions transport across cell membranes. These mutations cause the CFTR protein to be either absent or not function...
0 Anteile
932 Ansichten
0 Vorschau